Cardiac bridging integrator 1 gene therapy rescues chronic non-ischemic heart failure in minipigs. npj Regenerative Medicine , 2024; 9 (1) DOI: 10.1038/s41536-024-00380-0 Cite This Page : ...

Heart failure has historically been irreversible, but the outcome of a new study suggests that could someday change. At the University of Utah, scientists used a new gene therapy that was shown to ...

New Gene Therapy Reverses Heart Failure in Large Animal Model Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart ...

The new name draws from the company’s nearly two decades of work in ryanodine receptor (RyR) biology, which it has used to ...

A study published in Human Gene Therapy has involved the generation of a human monoclonal antibody (mAb) directed against ...

Treatments for rare diseases are hard to create and expensive to deliver, but there is new hope for editing the software of ...

Researchers have discovered that the protein Hmga1, found in zebrafish, can repair damaged mouse hearts by reactivating ...

The data suggests that Hmga1, a key protein for regenerating heart cells, could be a target for gene therapies that prevent cardiac failure.

While gene therapy has emerged as a promising alternative for treating beta-thalassemia, hematopoietic stem cell ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapie ...