Sangamo shares plunge after Pfizer ends hemophilia A gene therapy deal
Sangamo Therapeutics said on Monday that partner Pfizer has terminated their hemophilia A gene therapy co-development ...
Novartis gene therapy helps children with rare muscle disorder in study
Swiss drugmaker Novartis said on Monday its gene therapy helped improve motor function in children with a rare muscle ...
The American Journal of Managed Care2d
Gene Therapy Demonstrates High Efficacy in Severe β-Thalassemia
A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...
First of its kind gene therapy model offers hope for X-linked sideroblastic anemia treatment
Researchers at Children's Hospital of Philadelphia (CHOP) and the University of Pennsylvania Perelman School of Medicine ...
FierceBiotech3d
Pfizer cuts losses on near-approval hemophilia gene therapy, adding to troubled Sangamo's woes
Pfizer gave Sangamo Therapeutics coal for Christmas, terminating a hemophilia A gene therapy pact to deprive the ...
Hosted on MSN2d
What Is Minicircle? Bryan Johnson's Honduras Gene Therapy Company From Netflix's Don't Die Explained
The Man Who Wants to Live Forever introduced many viewers to the Minicircle company, and here's what the organization ...
Gene therapy treatment gives new hope to sickle cell patients
Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA ...
MM&M3d
Sangamo spirals after Pfizer halts hemophilia A gene therapy partnership
The pharma giant pulled out of its partnership with Sangamo, signalling unsteady waters for the latter company and the future ...
STAT5d
Pfizer kills hemophilia gene therapy deal, imperiling Sangamo
Sangamo, a gene therapy pioneer, loses a financial lifeline as Pfizer drops a gene therapy program for hemophilia.
Zacks.com on MSN5d
Novartis' Gene Therapy Meets Primary Endpoint in SMA Study
NVS' phase III study on experimental gene therapy candidate Intrathecal onasemnogene abeparvovec (OAV101IT) meets its primary ...
ophthalmologytimes1d
RESTORE study highlights persistent vision recovery in LHON patients with MT-ND4 mutation
The multinational, multicenter, prospective RESTORE Study is the 5-year follow-up study of the phase 3 clinical RESCUE and ...
Gene therapy research offers hope for people with chronic kidney disease
Researchers are making strides in improving gene therapies for genetic diseases, particularly chronic kidney disease, using adeno-associated virus, or AAV, vectors. While AAV-based treatments have ...